Patients and caregivers in the Pompe disease community are central to the development of potential new treatment options. If you have Pompe disease or live with and care for someone who does, we are looking to learn more about your experiences and perspective.
The results of this survey will help guide the development of patient support and awareness programs for current and future clinical trials.
In appreciation of your time, we will share with you a summary of the full results of this survey via email.
The survey is estimated to take 15 to 20 minutes of your time.